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Anatomical Therapeutic Chemical • A16AX28 • sepiapterin
A16AX03
sodium phenylbutyrate
Indicated for:
urea cycle disorders
A16AX04
nitisinone
Indicated for:
hereditary tyrosinemia type 1
A16AX05
zinc acetate
Indicated for:
mineral deficiency; mineral supplementation
A16AX06
miglustat
Indicated for:
Gaucher disease; Niemann-Pick type C disease
A16AX07
sapropterin
Indicated for:
phenylketonuria
A16AX08
teduglutide
Indicated for:
short bowel syndrome
A16AX10
eliglustat
Indicated for:
Gaucher disease
A16AX12
trientin
Indicated for:
Wilson disease
A16AX14
migalastat
Indicated for:
Fabry disease
A16AX15
telotristat
Indicated for:
carcinoid syndrome diarrhea
A16AX16
givosiran
Indicated for:
acute hepatic porphyria
A16AX18
lumasiran
Indicated for:
primary hyperoxaluria type 1
A16AX28
sepiapterin
Indicated for:
phenylketonuria