Active substance

Results for the substance glycerol phenylbutyrate

1 result

About this active substance

Glycerol phenylbutyrate is a medication used for the treatment of urea cycle disorders, a rare metabolic condition that leads to the accumulation of ammonia in the body. It works by facilitating the removal of ammonia through an alternative pathway.

The medication is administered orally, usually in the form of a solution, and is indicated for long-term use in patients with urea cycle disorders. It is important that treatment is monitored by a specialist.

Common side effects include nausea, vomiting, diarrhea, and abdominal pain. In rare cases, allergic reactions or changes in liver function may occur.

Glycerol phenylbutyrate is an essential therapeutic option for patients with urea cycle disorders, helping to prevent severe complications and improve quality of life.