Active substance

Results for the substance givosiran

1 result

About this active substance

Givosiran is a medication used for the treatment of acute hepatic porphyria, a rare genetic condition affecting heme metabolism. It reduces the frequency of acute attacks and the severity of symptoms.

This medication works by inhibiting the synthesis of an enzyme involved in heme production, thereby reducing the accumulation of toxic substances in the body. It is administered via subcutaneous injection, usually once a month.

Common side effects include nausea, fatigue, injection site reactions, and elevated liver enzyme levels. In rare cases, severe allergic reactions may occur.

It is important to follow your doctor's instructions and undergo regular tests to monitor the treatment's effects and prevent complications.