Active substance

Results for the substance patisiran

1 result

About this active substance

Patisiran is a medication used for the treatment of hereditary transthyretin-mediated amyloidosis (hATTR), a rare condition that affects the nerves and other organs. It is a small interfering RNA (siRNA) that reduces transthyretin production, slowing disease progression.

The medication is administered via intravenous infusion, as directed by your doctor. It is important to follow the administration schedule and monitor for any adverse reactions.

Side effects may include infusion site reactions, fatigue, nausea, or headache. In rare cases, severe allergic reactions or liver function impairment may occur.

Patients should inform their doctor about any other medications being used or pre-existing conditions to ensure the safe use of patisiran.