Active substance

Results for the substance nusinersen

3 results

About this active substance

Nusinersen is a medication used for the treatment of spinal muscular atrophy (SMA), a rare genetic disease that affects muscles and movement. It works by increasing the production of SMN (survival motor neuron) protein, which is essential for motor neuron function.

The medication is administered via intrathecal injection, following a specific schedule determined by the doctor. It is important to attend all scheduled administrations and monitoring appointments.

Side effects may include headache, nausea, back pain, or, in rare cases, severe allergic reactions.

Patients should inform their doctor about any other medications being used or pre-existing conditions to ensure the safe use of nusinersen.