Active substance

Results for the substance idursulfase

1 result

About this active substance

Idursulfase is a medication used to treat Hunter syndrome (mucopolysaccharidosis type II), a rare genetic disorder caused by a deficiency of the enzyme iduronate-2-sulfatase. It works by replacing the missing enzyme, helping to break down accumulated glycosaminoglycans in cells.

The medication is administered via intravenous infusion, usually once a week, under the supervision of a specialist.

Side effects may include infusion site reactions, fever, headache, or fatigue. In rare cases, severe allergic reactions may occur.

Patients should be closely monitored during treatment and inform their doctor about any other medications they are taking. Pregnant or breastfeeding women should consult a specialist before use.